(PharmaNewsWire.Com, August 31, 2017 ) Duchenne muscular dystrophy is a condition which causes muscle weakness. DMD is an X-linked disorder. The gene for DMD is present on the X chromosome. It codes for a protein named dystrophin. Dystrophin is essential for providing structural support inside muscle cells. Symptoms usually appear before age 6 and may appear as early as infancy. They include fatigue, learning difficulties, intellectual disability, muscle weakness and progressive difficulty walking.
Report Highlights
Global Markets Direct's Pharmaceutical and Healthcare latest pipeline guide Duchenne Muscular Dystrophy-Pipeline Review, H2 2017, provides comprehensive information on the therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders), complete with analysis by stage of development, drug target, mechanism of action (MoA), route of administration (RoA) and molecule type. The guide covers the descriptive pharmacological action of the therapeutics, its complete research and development history and latest news and press releases.
The Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide also reviews of key players involved in therapeutic development for Duchenne Muscular Dystrophy and features dormant and discontinued projects. The guide covers therapeutics under Development by Companies /Universities /Institutes, the molecules developed by Companies in Pre-Registration, Phase III, Phase II, Phase I, IND/CTA Filed, Preclinical and Discovery stages are 3, 4, 12, 11, 2, 53 and 15 respectively. Similarly, the Universities portfolio in Phase II, Phase I, Preclinical and Discovery stages comprises 1, 2, 8 and 1 molecules, respectively.
Duchenne Muscular Dystrophy (Genetic Disorders) pipeline guide helps in identifying and tracking emerging players in the market and their portfolios, enhances decision making capabilities and helps to create effective counter strategies to gain competitive advantage. The guide is built using data and information sourced from Global Markets Direct's proprietary databases, company/university websites, clinical trial registries, conferences, SEC filings, investor presentations and featured press releases from company/university sites and industry-specific third party sources. Additionally, various dynamic tracking processes ensure that the most recent developments are captured on a real time basis.
-The pipeline guide provides a snapshot of the global therapeutic landscape of Duchenne Muscular Dystrophy (Genetic Disorders). -The pipeline guide reviews pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders) by companies and universities/research institutes based on information derived from company and industry-specific sources. -The pipeline guide covers pipeline products based on several stages of development ranging from pre-registration till discovery and undisclosed stages. -The pipeline guide features descriptive drug profiles for the pipeline products which comprise, product description, descriptive licensing and collaboration details, R&D brief, MoA & other developmental activities. -The pipeline guide reviews key companies involved in Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics and enlists all their major and minor projects. -The pipeline guide evaluates Duchenne Muscular Dystrophy (Genetic Disorders) therapeutics based on mechanism of action (MoA), drug target, route of administration (RoA) and molecule type. -The pipeline guide encapsulates all the dormant and discontinued pipeline projects. -The pipeline guide reviews latest news related to pipeline therapeutics for Duchenne Muscular Dystrophy (Genetic Disorders)
-Procure strategically important competitor information, analysis, and insights to formulate effective R&D strategies. -Recognize emerging players with potentially strong product portfolio and create effective counter-strategies to gain competitive advantage. -Find and recognize significant and varied types of therapeutics under development for Duchenne Muscular Dystrophy (Genetic Disorders). -Classify potential new clients or partners in the target demographic. -Develop tactical initiatives by understanding the focus areas of leading companies. -Plan mergers and acquisitions meritoriously by identifying key players and it's most promising pipeline therapeutics. -Formulate corrective measures for pipeline projects by understanding Duchenne Muscular Dystrophy (Genetic Disorders) pipeline depth and focus of Indication therapeutics. -Develop and design in-licensing and out-licensing strategies by identifying prospective partners with the most attractive projects to enhance and expand business potential and scope. -Adjust the therapeutic portfolio by recognizing discontinued projects and understand from the know-how what drove them from pipeline.
Key Company profiles
4P-Pharma SAS Acceleron Pharma Inc Akashi Therapeutics Inc Antisense Therapeutics Ltd Asklepios BioPharmaceutical Inc Beech Tree Labs Inc Bioleaders Corp BioMarin Pharmaceutical Inc Capricor Therapeutics Inc Catabasis Pharmaceuticals Inc CRISPR Therapeutics Daiichi Sankyo Company Ltd Debiopharm International SA Editas Medicine Inc Eloxx Pharmaceuticals Ltd F. Hoffmann-La Roche Ltd FibroGen Inc Galapagos NV Genethon SA GTx Inc GW Pharmaceuticals Plc Italfarmaco SpA Karyopharm Therapeutics Inc La Jolla Pharmaceutical Company Lexicon Pharmaceuticals Inc Marathon Pharmaceuticals LLC
Number of Products under Development for Duchenne Muscular Dystrophy, H2 2017 Number of Products under Development by Companies, H2 2017 Number of Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Number of Products under Development by Companies, H2 2017 (Contd..2), H2 2017 Number of Products under Development by Companies, H2 2017 (Contd..3), H2 2017 Number of Products under Development by Universities/Institutes, H2 2017 Products under Development by Companies, H2 2017 Products under Development by Companies, H2 2017 (Contd..1), H2 2017 Products under Development by Companies, H2 2017 (Contd..2), H2 2017 Products under Development by Companies, H2 2017 (Contd..3), H2 2017 Products under Development by Companies, H2 2017 (Contd..4), H2 2017 Products under Development by Companies, H2 2017 (Contd..5), H2 2017 Products under Development by Universities/Institutes, H2 2017 Number of Products by Stage and Target, H2 2017 Number of Products by Stage and Target, H2 2017 (Contd..1), H2 2017 Number of Products by Stage and Mechanism of Action, H2 2017 Number of Products by Stage and Mechanism of Action, H2 2017 (Contd..1), H2 2017 Number of Products by Stage and Route of Administration, H2 2017 Number of Products by Stage and Molecule Type, H2 2017 Duchenne Muscular Dystrophy-Pipeline by 4P-Pharma SAS, H2 2017 Duchenne Muscular Dystrophy-Pipeline by Acceleron Pharma Inc, H2 2017 Duchenne Muscular Dystrophy-Pipeline by Akashi Therapeutics Inc, H2 2017 Duchenne Muscular Dystrophy-Pipeline by Antisense Therapeutics Ltd, H2 2017 Duchenne Muscular Dystrophy-Pipeline by Asklepios BioPharmaceutical Inc, H2 2017
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